Press Releases May 17, 2026 04:00 PM

Design Therapeutics to Host Investor Webcast to Review Data from RESTORE-FA Trial of DT-216P2 for Friedreich’s Ataxia on Monday, May 18, 2026

Design Therapeutics to present Phase 1/2 RESTORE-FA trial data for DT-216P2 in Friedreich’s Ataxia on May 18, 2026

By Derek Hwang
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DSGN

Design Therapeutics, a clinical-stage biotech company, will announce data from its ongoing Phase 1/2 RESTORE-FA trial evaluating DT-216P2, a novel GeneTAC® therapy candidate for treating Friedreich’s ataxia, on May 18, 2026. The company will host an investor webcast detailing these clinical results. Design Therapeutics utilizes its GeneTAC® platform to modulate gene expression for various genetic diseases, with additional programs targeting Fuchs endothelial corneal dystrophy, myotonic dystrophy type-1, and Huntington’s disease.

Design Therapeutics to Host Investor Webcast to Review Data from RESTORE-FA Trial of DT-216P2 for Friedreich’s Ataxia on Monday, May 18, 2026
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Key Points

  • Design Therapeutics will present data from the Phase 1/2 RESTORE-FA trial assessing DT-216P2 in Friedreich’s ataxia patients.
  • The company’s GeneTAC® platform enables targeted modulation of disease-related gene expression.
  • Design Therapeutics is advancing multiple genetic medicine programs beyond Friedreich’s ataxia, including Huntington’s disease and other degenerative conditions.

CARLSBAD, Calif., May 17, 2026 (GLOBE NEWSWIRE) -- Design Therapeutics, Inc. (Nasdaq: DSGN), a clinical-stage biotechnology company developing treatments for serious degenerative genetic diseases, will announce data from the ongoing Phase 1/2 RESTORE-FA trial evaluating DT-216P2 in patients with Friedreich’s ataxia (FA) on Monday, May 18, 2026. Management will host a conference call and webcast at 8:00 a.m. ET.

A live webcast of the presentation will be available here and in the investors section of the company’s website at www.designtx.com. The webcast will be archived for at least 30 days following the presentation.

About Design Therapeutics
Design Therapeutics is a clinical-stage biotechnology company developing a new class of therapies based on its platform of GeneTAC® gene targeted chimera small molecules. The company’s GeneTAC® molecules are designed to either dial up or dial down the expression of a specific disease-causing gene to address the underlying cause of disease. In addition to its clinical-stage GeneTAC® programs, DT-216P2, in development for patients with Friedreich ataxia, DT-168, for Fuchs endothelial corneal dystrophy, and DT-818, for myotonic dystrophy type-1, the company is advancing a program in Huntington’s disease. Discovery efforts are underway for multiple genomic medicines. For more information, please visit designtx.com.

Contact:
Renee Leck, THRUST
renee@thrustsc.com


Risks

  • As a clinical-stage biotech, outcomes of Phase 1/2 trials are uncertain and may not demonstrate efficacy or safety.
  • Regulatory approvals required for GeneTAC® therapies could face delays or denials impacting commercialization.
  • The niche market for rare genetic diseases may limit rapid revenue growth and broad market adoption.

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